16 published brand profiles in this category. Cite the individual brand profile for brand-specific facts.
4D Molecular Therapeutics - 4DMT is a clinical stage biopharma company inventing and developing innovative products to unlock the full potential of genetic medicine to treat large market diseases.
Abeona Therapeutics - Abeona Therapeutics is a gene therapy brand headquartered in New York, NY, founded in 2015.
AGTC - Beacon aids in restoring and improving the vision of patients with ophthalmic gene therapy. Find out more.
Audentes Therapeutics - Audentes Therapeutics is a gene therapy company headquartered in San Francisco, CA, founded in 2012.
Avrobio - Avrobio is a gene therapy company headquartered in Cambridge, MA, founded in 2015.
Encoded Therapeutics - Encoded Therapeutics is a gene therapy company headquartered in South San Francisco, CA, founded in 2017.
Generation Bio - Generation Bio is a gene therapy company headquartered in Cambridge, MA, founded in 2016.
GenSight Biologics - GenSight Biologics is a gene therapy company headquartered in Paris, France, founded in 2012.
Lysogene - Lysogene is a gene therapy company headquartered in Paris, France, founded in 2009.
MeiraGTx - Uniquely, MeiraGTx has developed a novel technology for in vivo delivery of any biologic therapeutic using oral small molecules. This transformative riboswitch gene regulation technology allows precise, dose-responsive control of gene expression by oral small molecules. MeiraGTx is focusing the riboswitch platform on the regulated in vivo delivery of metabolic peptides, including GLP-1, GIP, Glucagon, Amylin, PYY and Leptin, as well as cell therapy, CAR-T for liquid and solid tumors and autoimmu
Nightstar Therapeutics - Nightstar Therapeutics is a gene therapy company headquartered in London, UK, founded in 2013.
Regenxbio - Patients & Families Envisioning a brighter future for patients We know every day matters to patients and their families. That’s why we are innovating what is possible in gene therapy with the goal of delivering one-time treatments to patients living with common and rare diseases. Leading the Charge We’re pioneering a new field of discovery REGENXBIO is seeking to improve lives through the curative potential of gene therapy.
Sangamo Therapeutics - By translating our groundbreaking science into medicines we aim to transform patients’ lives by replacing today’s symptomatic treatments with tomorrow’s genomic cures.
Spark Therapeutics - At Genentech, we believe we can make a difference by delivering on Our Promise to improve the lives of patients and create healthier communities for all. You are encouraged to report negative side effects of prescription drugs to the FDA. Visit www.
uniQure - For more than two decades, we have been working tirelessly to harness the power of genomic medicine to deliver breakthrough treatments that change patients’ lives.
Voyager Therapeutics - At Voyager, our values are more than words; they define how we go about our work every day. As we work to create neurotherapeutics, we know that what we achieve and how we achieve it are equally important.